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- science.1242551 date "2013-08-22".
- science.1242551 doi "10.1126/science.1242551".
- science.1242551 first1 "I. M.".
- science.1242551 isCitedBy Genetic_disorder.
- science.1242551 issue "6148".
- science.1242551 journal "Science".
- science.1242551 last1 "Verma".
- science.1242551 pages "853–855".
- science.1242551 title "Gene Therapy That Works".
- science.1242551 volume "341".